Even though there are more FDA requirements to meet, today Sarepta Therapeutics "announced plans to submit a New Drug Application to the FDA for Eteplirsen for the treatment of Duchenne Muscular Dystrophy by year end 2014." Read more.
Other links with information.
Fox News Interview with Christine McShary & Jenn Mcnary
What this means for Aidan is that he'll likely be able to participate in this trial as Sarepta is taking boys who were in the drisapersen trial.
THIS IS VERY GOOD NEWS!!
Thanks to Mindy, Jenn, Christine, Tracy, and other DMD families who scheduled meetings with scientists and the FDA, and put together The Race to Yes campaign. There will certainly be more to do, but for today, a small celebration is in order!
9th Annual Run-Walk for Aidan & Runners Reunion
August 30, 2014
See photos from past runs.
to send for the site, please send them to Judy Schneider